• Tim

A cure to CMT 1A?

https://pubmed.ncbi.nlm.nih.gov/31713617/


A paper released in Jan 2020 demonstrated how a state of the art gene editing technique (CRISPR/Cas9) was able to eliminate CMT 1A from mice. This is amazing news for the community and hopefully is a bright future for everyone with CMT and potentially other genetic conditions.


Now as always there will be a few years before human trials, however these trials are expected to begin circa 2024 which would be fantastic. Also it is unknown as to whether this cure would prevent future damage or would rectify pre existing damage, so there is still a lot to watch for over the coming years!

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