CMT NEWS

The latest news on CMT treatments, trials and research.

Glial Cells Role in the Nervous System
Glial Cells Role in the Nervous System

September 8th, 2020

Glial cells play an active role in the nervous system

Pharnext and the Charcot-Marie-Tooth Association Enter Collaboration
Pharnext and the Charcot-Marie-Tooth Association Enter Collaboration

September 3rd, 2020

Pharnext and the Charcot-Marie-Tooth Association Enter Biomarker Research Collaboration

Pharnext PXT3003 Phase III Update
Pharnext PXT3003 Phase III Update

June 10th, 2020

Pharnext SA , a biopharmaceutical company, today provided an update on the regulatory and clinical status of PXT3003, its lead program in Charcot-Marie-Tooth Type 1A (“CMT1A”). PXT3003 is a novel drug candidate for the treatment of CMT1A and has...

Sarepta Therapeutics and Dyno Therapeutics to Develop Next-Generation Gene Therapy
Sarepta Therapeutics and Dyno Therapeutics to Develop Next-Generation Gene Therapy

May 11th 2020

Sarepta Therapeutics, Inc., the leader in precision genetic medicine for rare diseases, and Dyno Therapeutics, Inc., a biotech company applying artificial intelligence (AI) to gene therapy, today announced an agreement to develop next-generation A...

Regenacy Pharmaceuticals Raises $30 Million
Regenacy Pharmaceuticals Raises $30 Million

March 25th, 2020

Regenacy Pharmaceuticals, a clinical-stage biopharmaceutical company developing breakthrough treatments for diabetic and other peripheral neuropathies, today announced the closing of a $30 million Series A financing. The financing was co-led by Co...

Pharnext Announces PXT3003 for CMT-1A
Pharnext Announces PXT3003 for CMT-1A

March 18th, 2020

Pharnext, a biopharmaceutical company pioneering a new approach to developing innovative drug combinations based on big genomics data and artificial intelligence, today announced that the United Kingdom's Medicine and Healthcare products Regulator...